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Reactivation of γ-globin expression through Cas9 or base editor to treat β-hemoglobinopathies

  • Liren Wang
  • , Linxi Li
  • , Yanlin Ma
  • , Handan Hu
  • , Qi Li
  • , Yang Yang
  • , Wenbang Liu
  • , Shuming Yin
  • , Wei Li
  • , Bin Fu
  • , Ryo Kurita
  • , Yukio Nakamura
  • , Mingyao Liu*
  • , Yongrong Lai
  • , Dali Li
  • *此作品的通讯作者
  • East China Normal University
  • Hainan Medical University
  • The First Affiliated Hospital of Guangxi Medical University
  • Bioray Laboratories Inc.
  • Central South University
  • Japanese Red Cross Society
  • RIKEN

科研成果: 期刊稿件快报同行评审

源语言英语
页(从-至)276-278
页数3
期刊Cell Research
30
3
DOI
出版状态已出版 - 1 3月 2020

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