Waking up the silenced beauty: CRISPR/Cas9 mediated reactivation of fetal hemoglobin genes to treat severe beta-thalassemia in young patients

Liren Wang, Stefan Siwko, Dali Li

Research output: Contribution to journalArticlepeer-review

2 Scopus citations
Original languageEnglish
Article numberlnad009
JournalLife Medicine
Volume2
Issue number2
DOIs
StatePublished - 1 Apr 2023

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