Reactivation of γ-globin expression through Cas9 or base editor to treat β-hemoglobinopathies

  • Liren Wang
  • , Linxi Li
  • , Yanlin Ma
  • , Handan Hu
  • , Qi Li
  • , Yang Yang
  • , Wenbang Liu
  • , Shuming Yin
  • , Wei Li
  • , Bin Fu
  • , Ryo Kurita
  • , Yukio Nakamura
  • , Mingyao Liu*
  • , Yongrong Lai
  • , Dali Li
  • *Corresponding author for this work

Research output: Contribution to journalLetterpeer-review

69 Scopus citations
Original languageEnglish
Pages (from-to)276-278
Number of pages3
JournalCell Research
Volume30
Issue number3
DOIs
StatePublished - 1 Mar 2020

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